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news-medical.net
What is Exon Skipping?
Exon skipping has shown promise as a therapy for inherited conditions such as Duchenne muscular dystrophy.
May 7, 2021
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Overview of MET Amplification and MET Exon 14 Skipping Mutations in NSCLC | Targeted Oncology - Immunotherapy, Biomarkers, and Cancer Pathways
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0:16
156 reactions · 29 shares | Duchenne damages and weakens muscle cells over time. Exon-skipping therapies help the body build dystrophin—a protein muscles need to work properly. Learn more: https://bit.ly/3yV0bSJ | Sarepta Therapeutics | Facebook
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